Publications
- Anastasopoulou, S., Swann, G., Andres-Jensen, L., Attarbaschi, A., Barzilai-Birenboim, S., Erdelyi, D. J., Escherich, G., Hamadeh, L., Harila, A., Lopez-Lopez, E., McGowan, S., Moricke, A., Putti, C., Sagi, J. C., Schmiegelow, K., Ullrich, N. J., van der Sluis, I. M., Wahid, Q. U., Winick, N., Sramkova, L., Zalcberg, Y., Zapotocka, E., Bhojwani, D., Halsey, C., & Ponte Di Legno Neurotoxicity Working, G. (2024). Severe steroid-related neuropsychiatric symptoms during paediatric acute lymphoblastic leukaemia therapy-An observational Ponte di Legno Toxicity Working Group Study. Br J Haematol, PMID: 38924051 https://doi.org/10.1111/bjh.19610
- Bader, P., Potschger, U., Dalle, J. H., Moser, L. M., Balduzzi, A., Ansari, M., Buechner, J., Gungor, T., Ifversen, M., Krivan, G., Pichler, H., Renard, M., Staciuk, R., Sedlacek, P., Stein, J., Heusel, J. R., Truong, T., Wachowiak, J., Yesilipek, A., Locatelli, F., & Peters, C. (2024). Low rate of nonrelapse mortality in under-4-year-olds with ALL given chemotherapeutic conditioning for HSCT: a phase 3 FORUM study. Blood Adv, 8(2), 416-428, PMID: 37738088 https://doi.org/10.1182/bloodadvances.2023010591
- Beikbaghban, T., Proietti, L., Ebner, J., Sango, R., Rattei, T., Weichhart, T., Grebien, F., Sternberg, F., & Pohl, E. E. (2024). Differential regulation of mitochondrial uncoupling protein 2 in cancer cells. Biochim Biophys Acta Bioenerg, 1865(4), 149486, PMID: 38986826 https://doi.org/10.1016/j.bbabio.2024.149486
- Bellavia, D., Caruccio, S., Caradonna, F., Costa, V., Urzi, O., Raimondi, L., De Luca, A., Pagani, S., Naselli, F., & Giavaresi, G. (2024). Enzymatic TET-1 inhibition highlights different epigenetic behaviours of IL-1beta and TNFalpha in tumour progression of OS cell lines. Clin Epigenetics, 16(1), 136, PMID: 39358792 PMC11448002 https://doi.org/10.1186/s13148-024-01745-4
- Bertrums, E. J. M., de Kanter, J. K., Derks, L. L. M., Verheul, M., Trabut, L., van Roosmalen, M. J., Hasle, H., Antoniou, E., Reinhardt, D., Dworzak, M. N., Muhlegger, N., van den Heuvel-Eibrink, M. M., Zwaan, C. M., Goemans, B. F., & van Boxtel, R. (2024). Selective pressures of platinum compounds shape the evolution of therapy-related myeloid neoplasms. Nat Commun, 15(1), 6025, PMID: 39019934 PMC11255340 https://doi.org/10.1038/s41467-024-50384-z
- Bielack, S. S., Mettmann, V., Baumhoer, D., Blattmann, C., Burkhardt, B., Deinzer, C. K. W., Kager, L., Kevric, M., Mauz-Korholz, C., Muller-Abt, P., Reinhardt, D., Sabo, A. A., Schrappe, M., Sorg, B., Windhager, R., & Hecker-Nolting, S. (2024). Osteosarcoma Arising as a Secondary Malignancy following Treatment for Hematologic Cancer: A Report of 33 Affected Patients from the Cooperative Osteosarcoma Study Group (COSS). Cancers (Basel), 16(10), PMID: 38791915 PMC11120238 https://doi.org/10.3390/cancers16101836
- Bielack, S. S., Mettmann, V., Hecker-Nolting, S., Borkhardt, A., Hardes, J., Kager, L., von Kalle, T., Kevric, M., Koscielniak, E., Kratz, C. P., Kuhne, T., Nathrath, M., Rossig, C., Sorg, B., Sparber-Sauer, M., Werner, M., & Blattmann, C. (2024). Osteosarcoma as a secondary malignancy following rhabdomyosarcoma: A report of 28 affected patients from the Cooperative Osteosarcoma Study Group (COSS). Pediatr Blood Cancer, 71(12), e31344, PMID: 39344062 https://doi.org/10.1002/pbc.31344
- Buldini, B., Varotto, E., Maurer-Granofszky, M., Gaipa, G., Schumich, A., Bruggemann, M., Mejstrikova, E., Cazzaniga, G., Hrusak, O., Szczepanowski, M., Scarparo, P., Zimmermann, M., Strehl, S., Schinnerl, D., Zaliova, M., Karawajew, L., Bourquin, J. P., Feuerstein, T., Cario, G., Alten, J., Moricke, A., Biffi, A., Parasole, R., Fagioli, F., Valsecchi, M. G., Biondi, A., Locatelli, F., Attarbaschi, A., Schrappe, M., Conter, V., Basso, G., & Dworzak, M. N. (2024). CD371+ pediatric B-cell acute lymphoblastic leukemia: propensity to lineage switch and slow early response to treatment. Blood, PMID: 38215390 https://doi.org/10.1182/blood.2023021952
- Conter, V., Valsecchi, M. G., Cario, G., Zimmermann, M., Attarbaschi, A., Stary, J., Niggli, F., Dalla Pozza, L., Elitzur, S., Silvestri, D., Locatelli, F., Moricke, A., Engstler, G., Smisek, P., Bodmer, N., Barbaric, D., Izraeli, S., Rizzari, C., Boos, J., Buldini, B., Zucchetti, M., von Stackelberg, A., Matteo, C., Lehrnbecher, T., Lanvers-Kaminsky, C., Cazzaniga, G., Gruhn, B., Biondi, A., & Schrappe, M. (2024). Four Additional Doses of PEG-L-Asparaginase During the Consolidation Phase in the AIEOP-BFM ALL 2009 Protocol Do Not Improve Outcome and Increase Toxicity in High-Risk ALL: Results of a Randomized Study. J Clin Oncol, 42(8), 915-926, PMID: 38096462 https://doi.org/10.1200/JCO.23.01388
- Conter, V., Valsecchi, M. G., De Lorenzo, P., Gandemer, V., Heyman, M., Saha, V., Diaz, P., Li, C. K., Attarbaschi, A., Escherich, G., Stary, J., Schrappe, M., Pieters, R., Cario, G., & Biondi, A. (2024). No clear benefit of preventive cranial radiotherapy in childhood Philadelphia-positive acute lymphoblastic leukemia: a retrospective analysis of the EsPhALL2010 study. Haematologica, PMID: 39021218 https://doi.org/10.3324/haematol.2024.285253
- Corbacioglu, S., Lode, H., Ellinger, S., Zeman, F., Suttorp, M., Escherich, G., Bochennek, K., Gruhn, B., Lang, P., Rohde, M., Debatin, K. M., Steinbach, D., Beilken, A., Ladenstein, R., Spachtholz, R., Heiss, P., Hellwig, D., Troger, A., Koller, M., Menhart, K., Riemenschneider, M. J., Zoubaa, S., Kietz, S., Jakob, M., Sommer, G., Heise, T., Hundsdorfer, P., Kuhnle, I., Dilloo, D., Schonberger, S., Schwabe, G., von Luettichau, I., Graf, N., Schlegel, P. G., Fruhwald, M., Jorch, N., Paulussen, M., Schneider, D. T., Metzler, M., Leipold, A., Nathrath, M., Imschweiler, T., Christiansen, H., Schmid, I., Crazzolara, R., Niktoreh, N., Cario, G., Faber, J., Demmert, M., Babor, F., Frohlich, B., Bielack, S., Bernig, T., Greil, J., Eggert, A., Simon, T., & Foell, J. (2024). Irinotecan and temozolomide in combination with dasatinib and rapamycin versus irinotecan and temozolomide for patients with relapsed or refractory neuroblastoma (RIST-rNB-2011): a multicentre, open-label, randomised, controlled, phase 2 trial. Lancet Oncol, 25(7), 922-932, PMID: 38936379 https://doi.org/10.1016/S1470-2045(24)00202-X
- Cseh, A., Galimard, J. E., de la Fuente, J., Isgro, A., Zecca, M., Garwer, B., Biffi, A., Aljurf, M., Sundin, M., Belendez, C., Locatelli, F., Balduzzi, A., Lawson, S., Sengeloev, H., Ifversen, M., Saccardi, R., Wynn, R., Lankester, A. C., Corbacioglu, S., & Peters, C. (2024). Busulfan-fludarabine- or treosulfan-fludarabine-based conditioning before allogeneic HSCT from matched sibling donors in paediatric patients with sickle cell disease: A study on behalf of the EBMT Paediatric Diseases and Inborn Errors Working Parties. Br J Haematol, 204(1), e1-e5, PMID: 37795523 https://doi.org/10.1111/bjh.19122
- Damek, A., Kurch, L., Franke, F. C., Attarbaschi, A., Beishuizen, A., Cepelova, M., Ceppi, F., Daw, S., Dieckmann, K., Fernandez-Teijeiro, A., Feuchtinger, T., Flerlage, J. E., Fossa, A., Georgi, T. W., Hasenclever, D., Hraskova, A., Karlen, J., Klekawka, T., Kluge, R., Korholz, D., Landman-Parker, J., Leblanc, T., Mauz-Korholz, C., Metzler, M., Pears, J., Steglich, J., Uyttebroeck, A., Vordermark, D., Wallace, W. H., Wohlgemuth, W. A., & Stoevesandt, D. (2024). Hodgkin lymphoma: hypodense lesions in mediastinal masses. Sci Rep, 14(1), 14591, PMID: 38918503 PMC11199705 https://doi.org/10.1038/s41598-024-64253-8
- Dauber, E. M., Haas, O. A., Nebral, K., Gassner, C., Haslinger, S., Geyeregger, R., Hustinx, H., Lejon Crottet, S., Scharberg, E. A., Muller-Steinhardt, M., Schonbacher, M., Mayr, W. R., & Kormoczi, G. F. (2024). Body-wide chimerism and mosaicism are predominant causes of naturally occurring ABO discrepancies. Br J Haematol, 205(3), 1188-1196, PMID: 38973155 https://doi.org/10.1111/bjh.19618
- David, A. F., Heinzel, A., Kammer, M., Aschauer, C., Reindl-Schwaighofer, R., Hu, K., Chen, H. S., Muckenhuber, M., Kubetz, A., Weijler, A. M., Worel, N., Edinger, M., Berlakovich, G., Lion, T., Sykes, M., Wekerle, T., & Oberbauer, R. (2024). Combination cell therapy leads to clonal deletion of donor-specific T cells in kidney transplant recipients. EBioMedicine, 106, 105239, PMID: 38996766 https://doi.org/10.1016/j.ebiom.2024.105239
- de Beijer, I. A. E., van den Oever, S. R., Charalambous, E., Cangioli, G., Balaguer, J., Bardi, E., Alfes, M., Canete Nieto, A., Correcher, M., Pinto da Costa, T., Degelsegger-Marquez, A., Duster, V., Filbert, A. L., Grabow, D., Gredinger, G., Gsell, H., Haupt, R., van Helvoirt, M., Ladenstein, R., Langer, T., Laschkolnig, A., Muraca, M., Pluijm, S. M. F., Rascon, J., Schreier, G., Tomasikova, Z., Trauner, F., Trinkunas, J., Trunner, K., Uyttebroeck, A., Kremer, L. C. M., van der Pal, H. J. H., Chronaki, C., & PanCareSurPass, C. (2024). IT-Related Barriers and Facilitators to the Implementation of a New European eHealth Solution, the Digital Survivorship Passport (SurPass Version 2.0): Semistructured Digital Survey. J Med Internet Res, 26, e49910, PMID: 38696248 PMC11099813 https://doi.org/10.2196/49910
- De Sa Fernandes, C., Novoszel, P., Gastaldi, T., Krauss, D., Lang, M., Rica, R., Kutschat, A. P., Holcmann, M., Ellmeier, W., Seruggia, D., Strobl, H., & Sibilia, M. (2024). The histone deacetylase HDAC1 controls dendritic cell development and anti-tumor immunity. Cell Rep, 43(6), 114308, PMID: 38829740 https://doi.org/10.1016/j.celrep.2024.114308
- Dernovsek, J., Gorican, T., Gedgaudas, M., Zajec, Z., Urbancic, D., Jug, A., Skok, Z., Sturtzel, C., Distel, M., Grdadolnik, S. G., Babu, K., Panchamatia, A., Stachowski, T. R., Fischer, M., Ilas, J., Zubriene, A., Matulis, D., Zidar, N., & Tomasic, T. (2024). Hiding in plain sight: Optimizing topoisomerase IIalpha inhibitors into Hsp90beta selective binders. Eur J Med Chem, 280, 116934, PMID: 39388906 https://doi.org/10.1016/j.ejmech.2024.116934
- Dernovsek, J., Urbancic, D., Zajec, Z., Sturtzel, C., Grissenberger, S., Wenninger-Weinzierl, A., Gedgaudas, M., Zubriene, A., Gorican, T., Golic Grdadolnik, S., Skok, Z., Ilas, J., Distel, M., Zidar, N., & Tomasic, T. (2024). First dual inhibitors of human topoisomerase IIalpha and Hsp90 C-terminal domain inhibit the growth of Ewing sarcoma in vitro and in vivo. Bioorg Chem, 153, 107850, PMID: 39395321 https://doi.org/10.1016/j.bioorg.2024.107850
- Dernovsek, J., Zajec, Z., Poje, G., Urbancic, D., Sturtzel, C., Gorican, T., Grissenberger, S., Ciura, K., Wozinski, M., Gedgaudas, M., Zubriene, A., Grdadolnik, S. G., Mlinaric-Rascan, I., Rajic, Z., Cotman, A. E., Zidar, N., Distel, M., & Tomasic, T. (2024). Exploration and optimisation of structure-activity relationships of new triazole-based C-terminal Hsp90 inhibitors towards in vivo anticancer potency. Biomed Pharmacother, 177, 116941, PMID: 38889640 https://doi.org/10.1016/j.biopha.2024.116941
- Dick, L., Batista, P. R., Zaby, P., Manhart, G., Kopatz, V., Kogler, L., Pichler, V., Grebien, F., Bakos, V., Plosz, B. G., Kolev, N. Z., Kenner, L., Kirchner, B., & Holloczki, O. (2024). The adsorption of drugs on nanoplastics has severe biological impact. Sci Rep, 14(1), 25853, PMID: 39468142 https://doi.org/10.1038/s41598-024-75785-4
- Dobersberger, M., Sumesgutner, D., Zajc, C. U., Salzer, B., Laurent, E., Emminger, D., Sylvander, E., Lehner, E., Teufl, M., Seigner, J., Bobbili, M. R., Kunert, R., Lehner, M., & Traxlmayr, M. W. (2024). An engineering strategy to target activated EGFR with CAR T cells. Cell Rep Methods, 100728, PMID: 38492569 https://doi.org/10.1016/j.crmeth.2024.100728
- Edtmayer, S., Witalisz-Siepracka, A., Zdarsky, B., Heindl, K., Weiss, S., Eder, T., Dutta, S., Graichen, U., Klee, S., Sharif, O., Wieser, R., Gyorffy, B., Poli, V., Casanova, E., Sill, H., Grebien, F., & Stoiber, D. (2024). A novel function of STAT3beta in suppressing interferon response improves outcome in acute myeloid leukemia. Cell Death Dis, 15(5), 369, PMID: 38806478 PMC11133483 https://doi.org/10.1038/s41419-024-06749-9
- Elitzur, S., Shiloh, R., Loeffen, J. L. C., Pastorczak A Md, P., Takagi, M., Bomken, S., Baruchel, A., Lehrnbecher, T., Tasian, S. K., Abla, O., Arad-Cohen, N., Astigarraga, I., Ben-Harosh, M., Bodmer, N., Brozou, T., Ceppi, F., Chugaeva, L., Dalla-Pozza, L., Ducassou, S., Escherich, G., Farah, R., Gibson, A., Hasle, H., Hoveyan, J., Jacoby, E., Jazbec, J., Junk, S. V., Kolenova, A., Lazic, J., Lo Nigro, L., Mahlaoui, N., Miller, L. H., Papadakis, V. M. D. P., Pecheux, L., Pillon, M., Sarouk, I., Stary, J., Stiakaki, E., Strullu, M., Tran, T. H., Ussowicz, M., Verdu-Amoros, J., Wakulinska, A. Z., Zawitkowska, J., Stoppa-Lyonnet, D., Taylor, A. M., Shiloh, Y., Izraeli, S., Minard-Colin, V., Schmiegelow, K., Nirel, R., Attarbaschi, A., & Borkhardt, A. (2024). ATM germline pathogenic variants affect outcomes in children with ataxia-telangiectasia and hematological malignancies. Blood, PMID: 38917355 https://doi.org/10.1182/blood.2024024283
- Erlacher, M., Andresen, F., Sukova, M., Stary, J., De Moerloose, B., Bosch, J., Dworzak, M., Seidel, M. G., Polychronopoulou, S., Beier, R., Kratz, C. P., Nathrath, M., Fruhwald, M. C., Gohring, G., Bergmann, A. K., Mayerhofer, C., Lebrecht, D., Ramamoorthy, S., Yoshimi, A., Strahm, B., Wlodarski, M. W., & Niemeyer, C. M. (2024). Spontaneous remission and loss of monosomy 7: a window of opportunity for young children with SAMD9L syndrome. Haematologica, 109(2), 422-430, PMID: 37584291 PMC10828767 https://doi.org/10.3324/haematol.2023.283591
- Erman, B., Bal, S. K., Aydogmus, C., Ersoy, G. Z., & Boztug, K. (2024). A Novel Homozygous Six Base Pair Deletion Found in the NFATC2 Gene in a Patient with EBV-Associated Lymphoproliferation. J Clin Immunol, 44(3), 74, PMID: 38427060 PMC10907409 https://doi.org/10.1007/s10875-024-01675-z
- Fernandes, J. S., Blattmann, C., Hecker-Nolting, S., Kager, L., Kevric, M., Mettmann, V., Sorg, B., Fernandes, M., & Bielack, S. S. (2024). Beyond 5-year survival. A report from the Cooperative Osteosarcoma Study Group (COSS). Cancer Med, 13(1), e6893, PMID: 39102672 PMC10823757 https://doi.org/10.1002/cam4.6893
- Fernandez-Mateos, J.*, Cresswell, G. D.*, Trahearn, N.*, Webb, K., Sakr, C., Lampis, A., Stuttle, C., Corbishley, C. M., Stavrinides, V., Zapata, L., Spiteri, I., Heide, T., Gallagher, L., James, C., Ramazzotti, D., Gao, A., Kote-Jarai, Z., Acar, A., Truelove, L., Proszek, P., Murray, J., Reid, A., Wilkins, A., Hubank, M., Eeles, R., Dearnaley, D., & Sottoriva, A. (2024). Tumor evolution metrics predict recurrence beyond 10 years in locally advanced prostate cancer. Nat Cancer, PMID: 38997466 https://doi.org/10.1038/s43018-024-00787-0 * Shared first authorship
- Feuchtinger, T., Bader, P., Subklewe, M., Breidenbach, M., Willier, S., Metzler, M., Gokbuget, N., Hauer, J., Muller, F., Schlegel, P. G., Fruhwald, M., Schmid, C., Troeger, A., Baldus, C., Meisel, R., Kunkele, A., Topp, M., Bourquin, J. P., Cario, G., Von Stackelberg, A., & Peters, C. (2024). Approaches for bridging therapy prior to chimeric antigen receptor T cells for relapsed/refractory acute lymphoblastic B-lineage leukaemia in children and young adults. Haematologica, PMID: 38356450 https://doi.org/10.3324/haematol.2023.283780 (Online ahead of print)
- Filbert, A. L., Kremer, L., Ladenstein, R., Chronaki, C., Degelsegger-Marquez, A., van der Pal, H., Bardi, E., Uyttebroeck, A., Langer, T., Muraca, M., Nieto, A. C., Rascon, J., Bagnasco, F., Beyer, S., Te Dorsthorst, J., Essiaf, S., Galan, A. O., Kienesberger, A., O’Brien, K., Palau, M. C., Pluijm, S. M. F., di Profio, S., Saraceno, D., Schneider, C., Schreier, G., Trinkunas, J., Zamberlan, I., Grabow, D., Haupt, R., & PanCareSurPass, c. (2024). Scaling up and implementing the digital Survivorship Passport tool in routine clinical care – The European multidisciplinary PanCareSurPass project. Eur J Cancer, 202, 114029, PMID: 38513384 https://doi.org/10.1016/j.ejca.2024.114029
- Fink, F. M., Hopfl, R., Witsch-Baumgartner, M., Kropshofer, G., Martin, S., Fink, V., Heeg, M., Peters, C., Zschocke, J., & Haas, O. A. (2024). Retrospective identification of the first cord blood-transplanted severe aplastic anemia in a STAT1-associated chronic mucocutaneous candidiasis family: case report, review of literature and pathophysiologic background. Front Immunol, 15, 1430938, PMID: 39114664 PMC11303233 https://doi.org/10.3389/fimmu.2024.1430938
- Gargano, M. A., Matentzoglu, N., Coleman, B., Addo-Lartey, E. B., Anagnostopoulos, A. V., Anderton, J., Avillach, P., Bagley, A. M., Bakstein, E., Balhoff, J. P., Baynam, G., Bello, S. M., Berk, M., Bertram, H., Bishop, S., Blau, H., Bodenstein, D. F., Botas, P., Boztug, K., Cady, J., Callahan, T. J., Cameron, R., Carbon, S. J., Castellanos, F., Caufield, J. H., Chan, L. E., Chute, C. G., Cruz-Rojo, J., Dahan-Oliel, N., Davids, J. R., de Dieuleveult, M., de Souza, V., de Vries, B. B. A., de Vries, E., DePaulo, J. R., Derfalvi, B., Dhombres, F., Diaz-Byrd, C., Dingemans, A. J. M., Donadille, B., Duyzend, M., Elfeky, R., Essaid, S., Fabrizzi, C., Fico, G., Firth, H. V., Freudenberg-Hua, Y., Fullerton, J. M., Gabriel, D. L., Gilmour, K., Giordano, J., Goes, F. S., Moses, R. G., Green, I., Griese, M., Groza, T., Gu, W., Guthrie, J., Gyori, B., Hamosh, A., Hanauer, M., Hanusova, K., He, Y. O., Hegde, H., Helbig, I., Holasova, K., Hoyt, C. T., Huang, S., Hurwitz, E., Jacobsen, J. O. B., Jiang, X., Joseph, L., Keramatian, K., King, B., Knoflach, K., Koolen, D. A., Kraus, M. L., Kroll, C., Kusters, M., Ladewig, M. S., Lagorce, D., Lai, M. C., Lapunzina, P., Laraway, B., Lewis-Smith, D., Li, X., Lucano, C., Majd, M., Marazita, M. L., Martinez-Glez, V., McHenry, T. H., McInnis, M. G., McMurry, J. A., Mihulova, M., Millett, C. E., Mitchell, P. B., Moslerova, V., Narutomi, K., Nematollahi, S., Nevado, J., Nierenberg, A. A., Cajbikova, N. N., Nurnberger, J. I., Jr., Ogishima, S., Olson, D., Ortiz, A., Pachajoa, H., Perez de Nanclares, G., Peters, A., Putman, T., Rapp, C. K., Rath, A., Reese, J., Rekerle, L., Roberts, A. M., Roy, S., Sanders, S. J., Schuetz, C., Schulte, E. C., Schulze, T. G., Schwarz, M., Scott, K., Seelow, D., Seitz, B., Shen, Y., Similuk, M. N., Simon, E. S., Singh, B., Smedley, D., Smith, C. L., Smolinsky, J. T., Sperry, S., Stafford, E., Stefancsik, R., Steinhaus, R., Strawbridge, R., Sundaramurthi, J. C., Talapova, P., Tenorio Castano, J. A., Tesner, P., Thomas, R. H., Thurm, A., Turnovec, M., van Gijn, M. E., Vasilevsky, N. A., Vlckova, M., Walden, A., Wang, K., Wapner, R., Ware, J. S., Wiafe, A. A., Wiafe, S. A., Wiggins, L. D., Williams, A. E., Wu, C., Wyrwoll, M. J., Xiong, H., Yalin, N., Yamamoto, Y., Yatham, L. N., Yocum, A. K., Young, A. H., Yuksel, Z., Zandi, P. P., Zankl, A., Zarante, I., Zvolsky, M., Toro, S., Carmody, L. C., Harris, N. L., Munoz-Torres, M. C., Danis, D., Mungall, C. J., Kohler, S., Haendel, M. A., & Robinson, P. N. (2024). The Human Phenotype Ontology in 2024: phenotypes around the world. Nucleic Acids Res, 52(D1), D1333-D1346, PMID: 37953324 PMC10767975 https://doi.org/10.1093/nar/gkad1005
- Gazzarata, R., Strubin, M., Chronaki, C., Cangioli, G., Saraceno, D., Schreier, G., Beyer, S., Trauner, F., Gredinger, G., Ladenstein, R., Ae de Beijer, I., Cavalca, G., Trinkunas, J., Cervero Beltran, L., Vanautgaerden, M., Kock-Schoppenhauer, A. K., Neumann, A., Muraca, M., Filbert, A. L., Haupt, R., Grabow, D., & PanCareSurPass, C. (2024). Childhood Cancer Survivorship Passport Challenges in the European Health Data Space. Stud Health Technol Inform, 316, 1302-1306, PMID: 39176620 https://doi.org/10.3233/SHTI240651
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- L. Slamova, J. Starkova, E. Fronkova, M. Zaliova, L. Reznickova, F. W. van Delft, E. Vodickova, J. Volejnikova, Z. Zemanova, K. Polgarova, G. Cario, M. Figueroa, T. Kalina, K. Fiser, J. P. Bourquin, B. Bornhauser, M. Dworzak, J. Zuna, J. Trka, J. Stary, O. Hrusak, and E. Mejstrikova, ‘Cd2-Positive B-Cell Precursor Acute Lymphoblastic Leukemia with an Early Switch to the Monocytic Lineage’, Leukemia, 28 (2014), 609-20.
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- P. Valent, I. Sadovnik, Z. Racil, H. Herrmann, K. Blatt, S. Cerny-Reiterer, G. Eisenwort, T. Lion, T. Holyoake, and J. Mayer, ‘Dppiv (Cd26) as a Novel Stem Cell Marker in Ph+ Chronic Myeloid Leukaemia’, Eur J Clin Invest, 44 (2014), 1239-45.
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- A. Yoshimi, M. M. van den Heuvel-Eibrink, I. Baumann, S. Schwarz, I. Simonitsch-Klupp, P. de Paepe, V. Campr, G. B. Kerndrup, M. O’Sullivan, R. Devito, R. Leguit, M. Hernandez, M. Dworzak, B. de Moerloose, J. Stary, H. Hasle, O. P. Smith, M. Zecca, A. Catala, M. Schmugge, F. Locatelli, M. Fuhrer, A. Fischer, A. Guderle, P. Nollke, B. Strahm, and C. M. Niemeyer, ‘Comparison of Horse and Rabbit Antithymocyte Globulin in Immunosuppressive Therapy for Refractory Cytopenia of Childhood’, Haematologica, 99 (2014), 656-63.
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- R. Beier, A. Schulz, M. Honig, M. Eyrich, P. G. Schlegel, W. Holter, K. D. Stachel, K. Ehlert, J. Greil, W. Nurnberger, W. Wossmann, P. Bader, C. Urban, I. Muller, M. Suttorp, M. Sauer, B. Gruhn, R. Meisel, M. Zimmermann, and K. W. Sykora, ‘Long-Term Follow-up of Children Conditioned with Treosulfan: German and Austrian Experience’, Bone Marrow Transplant, 48 (2013), 491-501.
- S. Bilke, R. Schwentner, F. Yang, M. Kauer, G. Jug, R. L. Walker, S. Davis, Y. J. Zhu, M. Pineda, P. S. Meltzer, and H. Kovar, ‘Oncogenic Ets Fusions Deregulate E2f3 Target Genes in Ewing Sarcoma and Prostate Cancer’, Genome Res, 23 (2013), 1797-809.
- H. Boztug, A. Schumich, U. Potschger, N. Muhlegger, A. Kolenova, K. Reinhardt, and M. Dworzak, ‘Blast Cell Deficiency of Cd11a as a Marker of Acute Megakaryoblastic Leukemia and Transient Myeloproliferative Disease in Children with and without Down Syndrome’, Cytometry B Clin Cytom, 84 (2013), 370-8.
- F. Brackmann, M. Krumbholz, T. Langer, W. Rascher, W. Holter, and M. Metzler, ‘Novel Mll2 Mutation in Kabuki Syndrome with Hypogammaglobulinemia and Severe Chronic Thrombopenia’, J Pediatr Hematol Oncol, 35 (2013), e314-6.
- E. A. Coenen, C. M. Zwaan, D. Reinhardt, C. J. Harrison, O. A. Haas, V. de Haas, V. Mihal, B. De Moerloose, M. Jeison, J. E. Rubnitz, D. Tomizawa, D. Johnston, T. A. Alonzo, H. Hasle, A. Auvrignon, M. Dworzak, A. Pession, V. H. van der Velden, J. Swansbury, K. F. Wong, K. Terui, S. Savasan, M. Winstanley, G. Vaitkeviciene, M. Zimmermann, R. Pieters, and M. M. van den Heuvel-Eibrink, ‘Pediatric Acute Myeloid Leukemia with T(8;16)(P11;P13), a Distinct Clinical and Biological Entity: A Collaborative Study by the International-Berlin-Frankfurt-Munster Aml-Study Group’, Blood, 122 (2013), 2704-13.
- U. Creutzig, M. Zimmermann, J. P. Bourquin, M. N. Dworzak, G. Fleischhack, N. Graf, T. Klingebiel, B. Kremens, T. Lehrnbecher, C. von Neuhoff, J. Ritter, A. Sander, A. Schrauder, A. von Stackelberg, J. Stary, and D. Reinhardt, ‘Randomized Trial Comparing Liposomal Daunorubicin with Idarubicin as Induction for Pediatric Acute Myeloid Leukemia: Results from Study Aml-Bfm 2004’, Blood, 122 (2013), 37-43.
- U. Creutzig, M. Zimmermann, M. N. Dworzak, J. Ritter, G. Schellong, and D. Reinhardt, ‘Development of a Curative Treatment within the Aml-Bfm Studies’, Klin Padiatr, 225 Suppl 1 (2013), S79-86.
- T. M. Dantonello, C. Int-Veen, A. Schuck, G. Seitz, I. Leuschner, M. Nathrath, P. G. Schlegel, U. Kontny, W. Behnisch, I. Veit-Friedrich, S. Kube, E. Hallmen, B. Kazanowska, R. Ladenstein, M. Paulussen, G. Ljungman, S. S. Bielack, T. Klingebiel, E. Koscielniak, and Studiengruppe Cooperative Weichteilsarkom, ‘Survival Following Disease Recurrence of Primary Localized Alveolar Rhabdomyosarcoma’, Pediatr Blood Cancer, 60 (2013), 1267-73.
- C. Eckert, G. Henze, K. Seeger, N. Hagedorn, G. Mann, R. Panzer-Grumayer, C. Peters, T. Klingebiel, A. Borkhardt, M. Schrappe, A. Schrauder, G. Escherich, L. Sramkova, F. Niggli, J. Hitzler, and A. von Stackelberg, ‘Use of Allogeneic Hematopoietic Stem-Cell Transplantation Based on Minimal Residual Disease Response Improves Outcomes for Children with Relapsed Acute Lymphoblastic Leukemia in the Intermediate-Risk Group’, J Clin Oncol, 31 (2013), 2736-42.
- M. N. Gaze, T. Boterberg, K. Dieckmann, M. Hormann, J. E. Gains, K. P. Sullivan, and R. Ladenstein, ‘Results of a Quality Assurance Review of External Beam Radiation Therapy in the International Society of Paediatric Oncology (Europe) Neuroblastoma Group’s High-Risk Neuroblastoma Trial: A Siopen Study’, Int J Radiat Oncol Biol Phys, 85 (2013), 170-4.
- R. Geyeregger, C. Freimuller, S. Stevanovic, J. Stemberger, G. Mester, J. Dmytrus, T. Lion, H. G. Rammensee, G. Fischer, B. Eiz-Vesper, A. Lawitschka, S. Matthes, and G. Fritsch, ‘Short-Term in-Vitro Expansion Improves Monitoring and Allows Affordable Generation of Virus-Specific T-Cells against Several Viruses for a Broad Clinical Application’, PLoS One, 8 (2013), e59592.
- M. Ibrisimovic, D. Kneidinger, T. Lion, and R. Klein, ‘An Adenoviral Vector-Based Expression and Delivery System for the Inhibition of Wild-Type Adenovirus Replication by Artificial Micrornas’, Antiviral Res, 97 (2013), 10-23.
- M. Ibrisimovic, T. Lion, and R. Klein, ‘Combinatorial Targeting of 2 Different Steps in Adenoviral DNA Replication by Herpes Simplex Virus Thymidine Kinase and Artificial Microrna Expression for the Inhibition of Virus Multiplication in the Presence of Ganciclovir’, BMC Biotechnol, 13 (2013), 54.
- G. J. Kaspers, M. Zimmermann, D. Reinhardt, B. E. Gibson, R. Y. Tamminga, O. Aleinikova, H. Armendariz, M. Dworzak, S. Y. Ha, H. Hasle, L. Hovi, A. Maschan, Y. Bertrand, G. G. Leverger, B. I. Razzouk, C. Rizzari, P. Smisek, O. Smith, B. Stark, and U. Creutzig, ‘Improved Outcome in Pediatric Relapsed Acute Myeloid Leukemia: Results of a Randomized Trial on Liposomal Daunorubicin by the International Bfm Study Group’, J Clin Oncol, 31 (2013), 599-607.
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- R. Ladenstein, S. Weixler, B. Baykan, M. Bleeke, R. Kunert, D. Katinger, I. Pribill, P. Glander, S. Bauer, V. Pistoia, J. Michon, A. Garaventa, and H. N. Lode, ‘Ch14.18 Antibody Produced in Cho Cells in Relapsed or Refractory Stage 4 Neuroblastoma Patients: A Siopen Phase 1 Study’, MAbs, 5 (2013), 801-9.
- T. Lion, G. Webersinke, U. Kastner, C. Seger, G. Mitterbauer-Hohendanner, and G. Gastl, ‘[Current Diagnostic Requirements in Chronic Myeloid Leukemia]’, Wien Med Wochenschr, 163 (2013), 477-94.
- M. Ludwig, E. Enzenhofer, S. Schneider, M. Rauch, A. Bodenteich, K. Neumann, E. Prieschl-Grassauer, A. Grassauer, T. Lion, and C. A. Mueller, ‘Efficacy of a Carrageenan Nasal Spray in Patients with Common Cold: A Randomized Controlled Trial’, Respir Res, 14 (2013), 124.
- R. Luger, S. Valookaran, N. Knapp, C. Vizzardelli, A. M. Dohnal, and T. Felzmann, ‘Toll-Like Receptor 4 Engagement Drives Differentiation of Human and Murine Dendritic Cells from a Pro- into an Anti-Inflammatory Mode’, PLoS One, 8 (2013), e54879.
- S. Matthes-Martin, H. Boztug, and T. Lion, ‘Diagnosis and Treatment of Adenovirus Infection in Immunocompromised Patients’, Expert Rev Anti Infect Ther, 11 (2013), 1017-28.
- S. Matthes-Martin, A. Lawitschka, G. Fritsch, T. Lion, B. Grimm, S. Breuer, H. Boztug, S. Karlhuber, W. Holter, C. Peters, and M. Minkov, ‘Stem Cell Transplantation after Reduced-Intensity Conditioning for Sickle Cell Disease’, Eur J Haematol, 90 (2013), 308-12. E. Mayer, M. Holzl, S. Ahmadi, B. Dillinger, N. Pilat, D. Fuchs, T. Wekerle, and A. Heitger, ‘Ctla4-Ig Immunosuppressive Activity at the Level of Dendritic Cell/T Cell Crosstalk’, Int Immunopharmacol, 15 (2013), 638-45.
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- E. Muller, M. G. Seidel, H. Lackner, M. Dworzak, and C. Urban, ‘Acute Promyelocytic Leukemia Complicated by Massive Intracerebral Hemorrhage: Safety and Efficacy of Replacing Conventional Chemotherapy with Arsenic Trioxide in an Adolescent’, Klin Padiatr, 225 (2013), 172-3.
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- S. Preuner, and T. Lion, ‘Species-Specific Identification of a Wide Range of Clinically Relevant Fungal Pathogens by the Luminex((R)) Xmap Technology’, Methods Mol Biol, 968 (2013), 119-39.
- B. Reismuller, C. Peters, M. N. Dworzak, U. Potschger, C. Urban, B. Meister, K. Schmitt, K. Dieckmann, H. Gadner, A. Attarbaschi, G. Mann, and A. L. L. B. F. M. Study Group Austrian, ‘Outcome of Children and Adolescents with a Second or Third Relapse of Acute Lymphoblastic Leukemia (All): A Population-Based Analysis of the Austrian All-Bfm (Berlin-Frankfurt-Munster) Study Group’, J Pediatr Hematol Oncol, 35 (2013), e200-4. E. Salzer, S. Daschkey, S. Choo, M. Gombert, E. Santos-Valente, S. Ginzel, M. Schwendinger, O. A. Haas, G. Fritsch, W. F. Pickl, E. Forster-Waldl, A. Borkhardt, K. Boztug, K. Bienemann, and M. G. Seidel, ‘Combined Immunodeficiency with Life-Threatening Ebv-Associated Lymphoproliferative Disorder in Patients Lacking Functional Cd27’, Haematologica, 98 (2013), 473-8.
- E. Salzer, E. Santos-Valente, S. Klaver, S. A. Ban, W. Emminger, N. K. Prengemann, W. Garncarz, L. Mullauer, R. Kain, H. Boztug, A. Heitger, K. Arbeiter, F. Eitelberger, M. G. Seidel, W. Holter, A. Pollak, W. F. Pickl, E. Forster-Waldl, and K. Boztug, ‘B-Cell Deficiency and Severe Autoimmunity Caused by Deficiency of Protein Kinase C Delta’, Blood, 121 (2013), 3112-6.
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- R. K. Schultz, K. S. Baker, J. J. Boelens, C. M. Bollard, R. M. Egeler, M. Cowan, R. Ladenstein, A. Lankester, F. Locatelli, A. Lawitschka, J. E. Levine, M. Loh, E. Nemecek, C. Niemeyer, V. K. Prasad, V. Rocha, S. Shenoy, B. Strahm, P. Veys, D. Wall, P. Bader, S. A. Grupp, M. A. Pulsipher, and C. Peters, ‘Challenges and Opportunities for International Cooperative Studies in Pediatric Hematopoeitic Cell Transplantation: Priorities of the Westhafen Intercontinental Group’, Biol Blood Marrow Transplant, 19 (2013), 1279-87.
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- M. M. Strioga, T. Felzmann, D. J. Powell, Jr., V. Ostapenko, N. T. Dobrovolskiene, M. Matuskova, J. Michalek, and V. E. Schijns, ‘Therapeutic Dendritic Cell-Based Cancer Vaccines: The State of the Art’, Crit Rev Immunol, 33 (2013), 489-547.
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- T. Szczepanski, V. H. van der Velden, E. Waanders, R. P. Kuiper, P. Van Vlierberghe, B. Gruhn, C. Eckert, R. Panzer-Grumayer, G. Basso, H. Cave, U. Z. Stadt, D. Campana, A. Schrauder, R. Sutton, E. van Wering, J. P. Meijerink, and J. J. van Dongen, ‘Late Recurrence of Childhood T-Cell Acute Lymphoblastic Leukemia Frequently Represents a Second Leukemia Rather Than a Relapse: First Evidence for Genetic Predisposition’, J Clin Oncol, 29 (2011), 1643-9.
- D. R. Taggart, W. B. London, M. L. Schmidt, S. G. DuBois, T. F. Monclair, A. Nakagawara, B. De Bernardi, P. F. Ambros, A. D. Pearson, S. L. Cohn, and K. K. Matthay, ‘Prognostic Value of the Stage 4s Metastatic Pattern and Tumor Biology in Patients with Metastatic Neuroblastoma Diagnosed between Birth and 18 Months of Age’, J Clin Oncol, 29 (2011), 4358-64.
- U. Thiel, A. Wawer, P. Wolf, M. Badoglio, A. Santucci, T. Klingebiel, O. Basu, A. Borkhardt, H. J. Laws, Y. Kodera, A. Yoshimi, C. Peters, R. Ladenstein, A. Pession, A. Prete, E. C. Urban, W. Schwinger, P. Bordigoni, A. Salmon, M. A. Diaz, B. Afanasyev, I. Lisukov, E. Morozova, A. Toren, B. Bielorai, J. Korsakas, F. Fagioli, D. Caselli, G. Ehninger, B. Gruhn, U. Dirksen, F. Abdel-Rahman, M. Aglietta, E. Mastrodicasa, M. Torrent, P. Corradini, F. Demeocq, G. Dini, P. Dreger, M. Eyrich, J. Gozdzik, F. Guilhot, E. Holler, E. Koscielniak, C. Messina, D. Nachbaur, R. Sabbatini, E. Oldani, H. Ottinger, H. Ozsahin, R. Schots, S. Siena, J. Stein, S. Sufliarska, A. Unal, M. Ussowicz, P. Schneider, W. Woessmann, H. Jurgens, M. Bregni, S. Burdach, Party Solid Tumor Working, Blood the Pediatric DiseaseWorking Party of the European Group for, Transplantation Marrow, Blood Asia Pacific, Transplantation Marrow, Transplantations Pediatric Registry for Stem Cell, and Eicess Study Group Meta, ‘No Improvement of Survival with Reduced- Versus High-Intensity Conditioning for Allogeneic Stem Cell Transplants in Ewing Tumor Patients’, Ann Oncol, 22 (2011), 1614-21.
- M. van der Burg, H. Kreyenberg, A. Willasch, B. H. Barendregt, S. Preuner, F. Watzinger, T. Lion, E. Roosnek, J. Harvey, M. Alcoceba, M. G. Diaz, P. Bader, J. J. van Dongen, and E. U-supported EuroChimerism Consortium project QLRT, ‘Standardization of DNA Isolation from Low Cell Numbers for Chimerism Analysis by Pcr of Short Tandem Repeats’, Leukemia, 25 (2011), 1467-70. W. Warsch, K. Kollmann, E. Eckelhart, S. Fajmann, S. Cerny-Reiterer, A. Holbl, K. V. Gleixner, M. Dworzak, M. Mayerhofer, G. Hoermann, H. Herrmann, C. Sillaber, G. Egger, P. Valent, R. Moriggl, and V. Sexl, ‘High Stat5 Levels Mediate Imatinib Resistance and Indicate Disease Progression in Chronic Myeloid Leukemia’, Blood, 117 (2011), 3409-20.
- G. E. Winter, U. Rix, A. Lissat, A. Stukalov, M. K. Mullner, K. L. Bennett, J. Colinge, S. M. Nijman, S. Kubicek, H. Kovar, U. Kontny, and G. Superti-Furga, ‘An Integrated Chemical Biology Approach Identifies Specific Vulnerability of Ewing’s Sarcoma to Combined Inhibition of Aurora Kinases a and B’, Mol Cancer Ther, 10 (2011), 1846-56.
- V. Witt, E. Beiglbock, and G. Fritsch, ‘Bone Marrow Processing with the Amicus Separator System’, J Clin Apher, 26 (2011), 195-9.
- M. W. Wlodarski, J. Motter, T. A. Gorr, C. Olk-Batz, H. Hasle, M. Dworzak, C. M. Niemeyer, and C. Flotho, ‘Abnormal Promoter DNA Methylation in Juvenile Myelomonocytic Leukemia Is Not Caused by Mutation in Dnmt3a’, Blood, 118 (2011), 4490-1.
- D. N. Aryee, S. Niedan, M. Kauer, R. Schwentner, I. M. Bennani-Baiti, J. Ban, K. Muehlbacher, M. Kreppel, R. L. Walker, P. Meltzer, C. Poremba, R. Kofler, and H. Kovar, ‘Hypoxia Modulates Ews-Fli1 Transcriptional Signature and Enhances the Malignant Properties of Ewing’s Sarcoma Cells in Vitro’, Cancer Res, 70 (2010), 4015-23.
- A. Attarbaschi, M. Pisecker, A. Inthal, G. Mann, D. Janousek, M. Dworzak, U. Potschger, R. Ullmann, M. Schrappe, H. Gadner, O. A. Haas, R. Panzer-Grumayer, S. Strehl, and Group Austrian Berlin-Frankfurt-Munster Study, ‘Prognostic Relevance of Tlx3 (Hox11l2) Expression in Childhood T-Cell Acute Lymphoblastic Leukaemia Treated with Berlin-Frankfurt-Munster (Bfm) Protocols Containing Early and Late Re-Intensification Elements’, Br J Haematol, 148 (2010), 293-300.
- I. M. Bennani-Baiti, A. Cooper, E. R. Lawlor, M. Kauer, J. Ban, D. N. Aryee, and H. Kovar, ‘Intercohort Gene Expression Co-Analysis Reveals Chemokine Receptors as Prognostic Indicators in Ewing’s Sarcoma’, Clin Cancer Res, 16 (2010), 3769-78.
- M. Bruggemann, A. Schrauder, T. Raff, H. Pfeifer, M. Dworzak, O. G. Ottmann, V. Asnafi, A. Baruchel, R. Bassan, Y. Benoit, A. Biondi, H. Cave, H. Dombret, A. K. Fielding, R. Foa, N. Gokbuget, A. H. Goldstone, N. Goulden, G. Henze, D. Hoelzer, G. E. Janka-Schaub, E. A. Macintyre, R. Pieters, A. Rambaldi, J. M. Ribera, K. Schmiegelow, O. Spinelli, J. Stary, A. von Stackelberg, M. Kneba, M. Schrappe, J. J. van Dongen, Leukemia European Working Group for Adult Acute Lymphoblastic, and Group International Berlin-Frankfurt-Munster Study, ‘Standardized Mrd Quantification in European All Trials: Proceedings of the Second International Symposium on Mrd Assessment in Kiel, Germany, 18-20 September 2008’, Leukemia, 24 (2010), 521-35.
- M. Carlet, K. Janjetovic, J. Rainer, S. Schmidt, R. Panzer-Grumayer, G. Mann, M. Prelog, B. Meister, C. Ploner, and R. Kofler, ‘Expression, Regulation and Function of Phosphofructo-Kinase/Fructose-Biphosphatases (Pfkfbs) in Glucocorticoid-Induced Apoptosis of Acute Lymphoblastic Leukemia Cells’, BMC Cancer, 10 (2010), 638. V. Conter, C. R. Bartram, M. G. Valsecchi, A. Schrauder, R. Panzer-Grumayer, A. Moricke, M. Arico, M. Zimmermann, G. Mann, G. De Rossi, M. Stanulla, F. Locatelli, G. Basso, F. Niggli, E. Barisone, G. Henze, W. D. Ludwig, O. A. Haas, G. Cazzaniga, R. Koehler, D. Silvestri, J. Bradtke, R. Parasole, R. Beier, J. J. van Dongen, A. Biondi, and M. Schrappe, ‘Molecular Response to Treatment Redefines All Prognostic Factors in Children and Adolescents with B-Cell Precursor Acute Lymphoblastic Leukemia: Results in 3184 Patients of the Aieop-Bfm All 2000 Study’, Blood, 115 (2010), 3206-14.
- U. Creutzig, M. Zimmermann, M. Dworzak, C. Urban, G. Henze, B. Kremens, M. Lakomek, J. P. Bourquin, J. Stary, and D. Reinhardt, ‘Favourable Outcome of Patients with Childhood Acute Promyelocytic Leukaemia after Treatment with Reduced Cumulative Anthracycline Doses’, Br J Haematol, 149 (2010), 399-409.
- C. Diakos, S. Zhong, Y. Xiao, M. Zhou, G. M. Vasconcelos, G. Krapf, R. F. Yeh, S. Zheng, M. Kang, J. K. Wiencke, M. S. Pombo-de-Oliveira, R. Panzer-Grumayer, and J. L. Wiemels, ‘Tel-Aml1 Regulation of Survivin and Apoptosis Via Mirna-494 and Mirna-320a’, Blood, 116 (2010), 4885-93.
- M. N. Dworzak, G. Gaipa, A. Schumich, O. Maglia, R. Ratei, M. Veltroni, Z. Husak, G. Basso, L. Karawajew, H. Gadner, and A. Biondi, ‘Modulation of Antigen Expression in B-Cell Precursor Acute Lymphoblastic Leukemia During Induction Therapy Is Partly Transient: Evidence for a Drug-Induced Regulatory Phenomenon. Results of the Aieop-Bfm-All-Flow-Mrd-Study Group’, Cytometry B Clin Cytom, 78 (2010), 147-53.
- S. Ehlers, C. Herbst, M. Zimmermann, N. Scharn, M. Germeshausen, N. von Neuhoff, C. M. Zwaan, K. Reinhardt, I. H. Hollink, J. H. Klusmann, T. Lehrnbecher, S. Roettgers, J. Stary, M. Dworzak, K. Welte, U. Creutzig, and D. Reinhardt, ‘Granulocyte Colony-Stimulating Factor (G-Csf) Treatment of Childhood Acute Myeloid Leukemias That Overexpress the Differentiation-Defective G-Csf Receptor Isoform Iv Is Associated with a Higher Incidence of Relapse’, J Clin Oncol, 28 (2010), 2591-7.
- M. N. Gaze, T. Boterberg, K. Dieckmann, J. L. Habrand, S. Helfre, N. Peylan-Ramu, E. K. Chrzanowska, G. Schreier, and R. Ladenstein, ‘Development of an Electronic Database for Quality Assurance of Radiotherapy in the International Society of Paediatric Oncology (Europe) High Risk Neuroblastoma Study’, Radiother Oncol, 97 (2010), 593-5.
- H. Gerr, M. Zimmermann, M. Schrappe, M. Dworzak, W. D. Ludwig, J. Bradtke, A. Moericke, R. Schabath, U. Creutzig, and D. Reinhardt, ‘Acute Leukaemias of Ambiguous Lineage in Children: Characterization, Prognosis and Therapy Recommendations’, Br J Haematol, 149 (2010), 84-92.
- A. Handisurya, C. Schellenbacher, B. Reininger, F. Koszik, P. Vyhnanek, A. Heitger, R. Kirnbauer, and E. Forster-Waldl, ‘A Quadrivalent Hpv Vaccine Induces Humoral and Cellular Immune Responses in Whim Immunodeficiency Syndrome’, Vaccine, 28 (2010), 4837-41.
- L. Hertzberg, E. Vendramini, I. Ganmore, G. Cazzaniga, M. Schmitz, J. Chalker, R. Shiloh, I. Iacobucci, C. Shochat, S. Zeligson, G. Cario, M. Stanulla, S. Strehl, L. J. Russell, C. J. Harrison, B. Bornhauser, A. Yoda, G. Rechavi, D. Bercovich, A. Borkhardt, H. Kempski, G. te Kronnie, J. P. Bourquin, E. Domany, and S. Izraeli, ‘Down Syndrome Acute Lymphoblastic Leukemia, a Highly Heterogeneous Disease in Which Aberrant Expression of Crlf2 Is Associated with Mutated Jak2: A Report from the International Bfm Study Group’, Blood, 115 (2010), 1006-17.
- Z. Husak, D. Printz, A. Schumich, U. Potschger, and M. N. Dworzak, ‘Death Induction by Cd99 Ligation in Tel/Aml1-Positive Acute Lymphoblastic Leukemia and Normal B Cell Precursors’, J Leukoc Biol, 88 (2010), 405-12.
- C. Hutter, A. Attarbaschi, S. Fischer, C. Meyer, M. Dworzak, M. Konig, R. Marschalek, G. Mann, O. A. Haas, and E. R. Panzer-Grumayer, ‘Acute Monocytic Leukaemia Originating from Mll-Mllt3-Positive Pre-B Cells’, Br J Haematol, 150 (2010), 621-3.
- X. Jiang, Y. Gwye, D. Russell, C. Cao, D. Douglas, L. Hung, H. Kovar, T. J. Triche, and E. R. Lawlor, ‘Cd133 Expression in Chemo-Resistant Ewing Sarcoma Cells’, BMC Cancer, 10 (2010), 116. B. Jurgens, D. Fuchs, J. Reichenbach, and A. Heitger, ‘Intact Indoleamine 2,3-Dioxygenase Activity in Human Chronic Granulomatous Disease’, Clin Immunol, 137 (2010), 1-4.
- B. Jurgens, J. Raberger, D. Fuchs, and A. Heitger, ‘Indoleamine 2,3-Dioxygenase in Human Hematopoietic Stem Cell Transplantation’, Int J Tryptophan Res, 3 (2010), 77-90.
- H. Kovar, ‘Aurka Inhibitors: Right in Time’, Pediatr Blood Cancer, 55 (2010), 3-4. H. Kovar, ‘Downstream Ews/Fli1 – Upstream Ewing’s Sarcoma’, Genome Med, 2 (2010), 8.
- A. Kowalska, E. Bozsaky, and P. F. Ambros, ‘Sequence-Based High Resolution Chromosomal Comparative Genomic Hybridization (Cgh)’, Methods Mol Biol, 659 (2010), 299-312.
- R. Ladenstein, U. Potschger, M. C. Le Deley, J. Whelan, M. Paulussen, O. Oberlin, H. van den Berg, U. Dirksen, L. Hjorth, J. Michon, I. Lewis, A. Craft, and H. Jurgens, ‘Primary Disseminated Multifocal Ewing Sarcoma: Results of the Euro-Ewing 99 Trial’, J Clin Oncol, 28 (2010), 3284-91.
- R. Ladenstein, D. Valteau-Couanet, P. Brock, I. Yaniv, V. Castel, G. Laureys, J. Malis, V. Papadakis, A. Lacerda, E. Ruud, P. Kogner, M. Garami, W. Balwierz, H. Schroeder, M. Beck-Popovic, G. Schreier, D. Machin, U. Potschger, and A. Pearson, ‘Randomized Trial of Prophylactic Granulocyte Colony-Stimulating Factor During Rapid Cojec Induction in Pediatric Patients with High-Risk Neuroblastoma: The European Hr-Nbl1/Siopen Study’, J Clin Oncol, 28 (2010), 3516-24.
- C. Landlinger, S. Preuner, L. Baskova, M. van Grotel, N. G. Hartwig, M. Dworzak, G. Mann, A. Attarbaschi, L. Kager, C. Peters, S. Matthes-Martin, A. Lawitschka, M. M. van den Heuvel-Eibrink, and T. Lion, ‘Diagnosis of Invasive Fungal Infections by a Real-Time Panfungal Pcr Assay in Immunocompromised Pediatric Patients’, Leukemia, 24 (2010), 2032-8.
- M. C. Le Deley, O. Delattre, K. L. Schaefer, S. A. Burchill, G. Koehler, P. C. Hogendoorn, T. Lion, C. Poremba, J. Marandet, S. Ballet, G. Pierron, S. C. Brownhill, M. Nesslbock, A. Ranft, U. Dirksen, O. Oberlin, I. J. Lewis, A. W. Craft, H. Jurgens, and H. Kovar, ‘Impact of Ews-Ets Fusion Type on Disease Progression in Ewing’s Sarcoma/Peripheral Primitive Neuroectodermal Tumor: Prospective Results from the Cooperative Euro-E.W.I.N.G. 99 Trial’, J Clin Oncol, 28 (2010), 1982-8.
- T. Lion, K. Kosulin, C. Landlinger, M. Rauch, S. Preuner, D. Jugovic, U. Potschger, A. Lawitschka, C. Peters, G. Fritsch, and S. Matthes-Martin, ‘Monitoring of Adenovirus Load in Stool by Real-Time Pcr Permits Early Detection of Impending Invasive Infection in Patients after Allogeneic Stem Cell Transplantation’, Leukemia, 24 (2010), 706-14. K. K. Matthay, B. Shulkin, R. Ladenstein, J. Michon, F. Giammarile, V. Lewington, A. D. Pearson, and S. L. Cohn, ‘Criteria for Evaluation of Disease Extent by (123)I-Metaiodobenzylguanidine Scans in Neuroblastoma: A Report for the International Neuroblastoma Risk Group (Inrg) Task Force’, Br J Cancer, 102 (2010), 1319-26.
- A. L. Petzer, D. Wolf, D. Fong, T. Lion, I. Dyagil, Z. Masliak, A. Bogdanovic, L. Griskevicius, S. Lejniece, S. Goranov, L. Gercheva, A. Stojanovic, D. Peytchev, N. Tzvetkov, R. Griniute, R. Oucheva, H. Ulmer, M. Kwakkelstein, F. Rancati, and G. Gastl, ‘High-Dose Imatinib Improves Cytogenetic and Molecular Remissions in Patients with Pretreated Philadelphia-Positive, Bcr-Abl-Positive Chronic Phase Chronic Myeloid Leukemia: First Results from the Randomized Celsg Phase Iii Cml 11 “Istahit” Study’, Haematologica, 95 (2010), 908-13.
- H. Pichler, A. Moricke, G. Mann, A. Teigler-Schlegel, F. Niggli, K. Nebral, M. Konig, A. Inthal, D. Krehan, M. N. Dworzak, D. Janousek, J. Harbott, M. Schrappe, H. Gadner, S. Strehl, O. A. Haas, R. Panzer-Grumayer, A. Attarbaschi, and Group Berlin-Frankfurt-Munster Study, ‘Prognostic Relevance of Dic(9;20)(P11;Q13) in Childhood B-Cell Precursor Acute Lymphoblastic Leukaemia Treated with Berlin-Frankfurt-Munster (Bfm) Protocols Containing an Intensive Induction and Post-Induction Consolidation Therapy’, Br J Haematol, 149 (2010), 93-100.
- P. Rhein, R. Mitlohner, G. Basso, G. Gaipa, M. N. Dworzak, R. Kirschner-Schwabe, C. Hagemeier, M. Stanulla, M. Schrappe, W. D. Ludwig, L. Karawajew, and R. Ratei, ‘Cd11b Is a Therapy Resistance- and Minimal Residual Disease-Specific Marker in Precursor B-Cell Acute Lymphoblastic Leukemia’, Blood, 115 (2010), 3763-71.
- A. Sander, M. Zimmermann, M. Dworzak, G. Fleischhack, C. von Neuhoff, D. Reinhardt, G. J. Kaspers, and U. Creutzig, ‘Consequent and Intensified Relapse Therapy Improved Survival in Pediatric Aml: Results of Relapse Treatment in 379 Patients of Three Consecutive Aml-Bfm Trials’, Leukemia, 24 (2010), 1422-8.
- J. Santos, N. Cerveira, S. Bizarro, F. R. Ribeiro, C. Correia, L. Torres, S. Lisboa, J. Vieira, J. M. Mariz, L. Norton, S. Snijder, C. H. Mellink, A. Buijs, L. Y. Shih, S. Strehl, F. Micci, S. Heim, and M. R. Teixeira, ‘Expression Pattern of the Septin Gene Family in Acute Myeloid Leukemias with and without Mll-Sept Fusion Genes’, Leuk Res, 34 (2010), 615-21.
- M. G. Seidel, E. Grohmann, K. Sadeghi, A. Pollak, A. Heitger, and E. Forster-Waldl, ‘Vaccination against Tick-Borne Encephalitis Virus Tests Specific Igg Production Ability in Patients under Immunoglobulin Substitution Therapy’, Vaccine, 28 (2010), 6621-6.
- E. Sieczkowski, C. Lehner, P. F. Ambros, and M. Hohenegger, ‘Double Impact on P-Glycoprotein by Statins Enhances Doxorubicin Cytotoxicity in Human Neuroblastoma Cells’, Int J Cancer, 126 (2010), 2025-35. M. Steiner, A. Attarbaschi, M. Dworzak, H. Strobl, W. Pickl, R. Kornmuller, O. Haas, H. Gadner, G. Mann, and Group Austrian Berlin-Frankfurt-Munster Study, ‘Cytochemically Myeloperoxidase Positive Childhood Acute Leukemia with Lymphoblastic Morphology Treated as Lymphoblastic Leukemia’, J Pediatr Hematol Oncol, 32 (2010), e4-7.
- J. Stemberger, V. Witt, D. Printz, R. Geyeregger, and G. Fritsch, ‘Novel Single-Platform Multiparameter Fcm Analysis of Apoptosis: Significant Differences between Wash and No-Wash Procedure’, Cytometry A, 77 (2010), 1075-81.
- C. T. Storlazzi, A. Lonoce, M. C. Guastadisegni, D. Trombetta, P. D’Addabbo, G. Daniele, A. L’Abbate, G. Macchia, C. Surace, K. Kok, R. Ullmann, S. Purgato, O. Palumbo, M. Carella, P. F. Ambros, and M. Rocchi, ‘Gene Amplification as Double Minutes or Homogeneously Staining Regions in Solid Tumors: Origin and Structure’, Genome Res, 20 (2010), 1198-206.
- M. W. Traxlmayr, D. Wesch, A. M. Dohnal, P. Funovics, M. B. Fischer, D. Kabelitz, and T. Felzmann, ‘Immune Suppression by Gammadelta T-Cells as a Potential Regulatory Mechanism after Cancer Vaccination with Il-12 Secreting Dendritic Cells’, J Immunother, 33 (2010), 40-52.
- P. Van Vlierberghe, T. Palomero, H. Khiabanian, J. Van der Meulen, M. Castillo, N. Van Roy, B. De Moerloose, J. Philippe, S. Gonzalez-Garcia, M. L. Toribio, T. Taghon, L. Zuurbier, B. Cauwelier, C. J. Harrison, C. Schwab, M. Pisecker, S. Strehl, A. W. Langerak, J. Gecz, E. Sonneveld, R. Pieters, E. Paietta, J. M. Rowe, P. H. Wiernik, Y. Benoit, J. Soulier, B. Poppe, X. Yao, C. Cordon-Cardo, J. Meijerink, R. Rabadan, F. Speleman, and A. Ferrando, ‘Phf6 Mutations in T-Cell Acute Lymphoblastic Leukemia’, Nat Genet, 42 (2010), 338-42.
- C. von Neuhoff, D. Reinhardt, A. Sander, M. Zimmermann, J. Bradtke, D. R. Betts, Z. Zemanova, J. Stary, J. P. Bourquin, O. A. Haas, M. N. Dworzak, and U. Creutzig, ‘Prognostic Impact of Specific Chromosomal Aberrations in a Large Group of Pediatric Patients with Acute Myeloid Leukemia Treated Uniformly According to Trial Aml-Bfm 98’, J Clin Oncol, 28 (2010), 2682-9.
- C. M. Zwaan, D. Reinhardt, M. Zimmerman, H. Hasle, J. Stary, B. Stark, M. Dworzak, U. Creutzig, G. J. Kaspers, and B. F. M. Study Group on Paediatric A. M. L. International, ‘Salvage Treatment for Children with Refractory First or Second Relapse of Acute Myeloid Leukaemia with Gemtuzumab Ozogamicin: Results of a Phase Ii Study’, Br J Haematol, 148 (2010), 768-76.